Platforms & Performance
Celerion’s rapidly expanding gene therapy focus supports our clients’ bioanalytical needs for drug development by utilizing our international laboratories and top-fight scientists.
Gene Therapy
The Evolving Role of Gene Therapy in Drug Development
Gene therapy medicinal products (GTMPs) generally consist of a vector or delivery formulation/ system with an expressed therapeutic sequence including a genetic construct expressing therapeutic sequence or protein used to therapeutically target a genetic sequence for regulation, repair, addition or deletion.
Gene Therapy Product Support for:
- siRNA, RNA and DNA and Oligos
- Encapsulated and naked plasmids and mRNAs
- Viral vectors (adenovirus vectors (AdVs), adeno-associated virus vectors (AAVs), baculoviral vectors (BVs) and lentivirus vectors (LV))
Bioanalytical Strategy for Gene Therapy Product Development
Download PDF